Duchenne muscular dystrophy causes progressive muscle degeneration and weakness, but physical exercise should still be part of a comprehensive treatment strategy. Duchenne muscular dystrophy (DMD) is ...
Symptoms of DMD start in early childhood. Often, the first noticeable sign is a delay in reaching developmental milestones, like walking well by 18 months of age or sitting or standing without ...
Sarepta's EMBARK trial showed no significant improvement in motor function, despite some secondary benefits and no new safety concerns. Pfizer's CIFFREO trial also failed to meet its primary endpoint, ...
Duchenne muscular dystrophy (DMD) is an inherited muscle disorder that causes progressive breakdown of muscle tissue. Symptoms typically begin in early childhood, and most parents and caregivers ...
Duchenne muscular dystrophy (DMD) results from changes in the DMD gene. Children may inherit DMD gene changes from their parents or have spontaneous gene changes. The DMD gene tells the body how to ...