An infant named KJ Muldoon, born with a severe and typically fatal genetic disorder called CPS1 deficiency, is now walking and talking after receiving a one-of-a-kind, patient-specific gene-editing ...

A lot of effort has gone into finding ways to minimize or eliminate off-target edits. In a recent issue of Nature, ...

Small RNAs (sRNAs), traditionally regarded as noncoding post-transcriptional regulators, are increasingly recognised as ...